Orphan medicines in the EU – leaving no-one behind

December 21, 2017 – There are over 6,000 rare diseases and it is estimated that around 30 million people in the European Union (EU) suffer from one of them. Treating these patients can be very difficult, because there are only few medicines available. This represents a huge unmet medical need and a significant public health challenge. The EU’s orphan designation programme was launched in the year 2000 to encourage companies to research and develop … (leggi tutto)